Impressive progress has been made in the treatment of haemophilia using gene therapy.令人印象深刻的進展已取得在治療血友病的基因治療使用。


Professor Katherine High, a leading researcher from Philadelphia USA, is examining the obstacles to successful gene therapy in human patients with haemophilia.教授凱瑟琳高，領導這項研究由美國費城，現正研究的障礙，成功的基因治療在人類血友病患者。

Gene therapy has already been used to successfully treat haemophilia in mice and dogs.基因療法已經被用來成功地治療血友病在小鼠和狗。

“It has taken approximately 5 - 8 years to move from a cure for haemophilia in mice to a cure in dogs. “它已採取了大約5 -8年，從治療血友病，在小鼠的治愈率在狗。 This has been achieved by multiple gene transfer strategies.這已取得了由多個基因轉移的戰略。 Clinical studies have identified which aspects of gene transfer therapy in dogs are directly applicable in humans and have identified potential problems, such as mode of delivery, which must be overcome before applying this approach in humans,” said High.臨床研究已確定哪些方面的基因轉移治療的狗是直接適用於人類，並已確定了潛在的問題，如分娩方式，必須加以克服，然後再應用這種方法在人類，說： “高。

Source:資料來源： The Stem Cell Blog幹細胞博客